Towards a Gene Editing Approach for Mitochondrial NeuroGastroIntestinal Encephalomyopathy (MNGIE)

Marta Pares, Cristina Fornaguera, Ferran Vila, Sejin Oh, Steven H. Y. Fan, Ying K. Tam, Natalia Comes, Francisco Vidal, Salvador Borros, Jordi Barquinero

Research output: Indexed journal article Meeting Abstractpeer-review

Original languageEnglish
Pages (from-to)261-262
Number of pages2
JournalMolecular Therapy
Volume29
Issue number4
DOIs
Publication statusPublished - 27 Apr 2021

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